A gene-targeted therapy for a common subtype of acute
myeloid leukemia (AML) known as FLT-positive AML in which there is a FLT3 receptor
mutation. The FLT-3 inhibitor is a tyrosine kinase inhibitor that interferes with
abnormal FLT3 function by preventing essential proteins from binding to the DNA.
The FLT-3 inhibitor blocks the action of the altered FLT-3 gene, rendering it powerless.
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